miREX

Publications

Przanowski P, Wasko U, Zheng Z, Yu J, Sherman R, Zhu LJ, McConnell MJ, Tushir-Singh J, Green MR, Bhatnagar S. Pharmacological reactivation of inactive X-linked Mecp2 in cerebral cortical neurons of living mice. Proceedings of the National Academy of Sciences of the USA, 2018.

Posters & Presentations

Powers S*, Lou S, Nardini S, Likhite S, Sierra-Delgado JA, Baird M, Roussel F, Kaleem A, Schwartz M, Ray S, Bhatnagar S, Meyer K. A novel gene therapy for Rett Syndrome through reactivation of the silent X chromosome. Presented at the 25th American Society of Gene and Cell Therapy (ASGCT) Annual Meeting, 2022. *Received Excellence in Research Award

Relevant Scientific Publications

Vacca M, Della Ragione F, Scalabrì F, D'Esposito M. X inactivation and reactivation in X-linked diseases. Seminars in Cell and Developmental Biology, 2016.