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In vivo performance of a microfabricated catheter for intraparenchymal delivery
Human in silico trials for parametric computational fluid dynamics investigation of cerebrospinal fluid drug delivery: impact of injection location, injection protocol, and physiology.
Regulatory & supply chain implications for plasmids as critical starting materials in the manufacture of viral vector gene therapy products.
Pharmacological reactivation of inactive X-linked Mecp2 in cerebral cortical neurons of living mice.
Investigation of Human Intrathecal Solute Transport Dynamics Using a Novel in vitro Cerebrospinal Fluid System Analog.
Non-invasive MRI quantification of cerebrospinal fluid dynamics in amyotrophic lateral sclerosis patients.
In vitro and numerical simulation of blood removal from cerebrospinal fluid: comparison of lumbar drain to Neurapheresis therapy.
Single-dose gene-replacement therapy for Spinal Muscular Atrophy