About
Scientific Advisors

Isabelle Aubert, PhD
Senior Scientist, Sunnybrook Research Institute, University of Toronto
Maurizio Pellechia, PhD
Director, Center for Molecular and Translational Medicine, University of California, Riverside
Sanchita Bhatnagar, PhD
Associate Professor, University of California, Davis
Nicolas Wein, PhD
Principal Investigator, Abigail Wexner Research Institute, Nationwide Children’s Hospital
Laura Ferraiuolo, PhD
Lecturer in Translational Neurobiology, Department of Neuroscience, University of Sheffield
Dave Arnold, MD
Associate Professor, Division of Neuromuscular Disease, Department of Neurology, Department of PM&R, and Department of Neuroscience
The Ohio State Wexner Medical Center
The Ohio State Wexner Medical Center
Timothy Benke, MD, PhD
Professor, Pediatrics-Neurology, School of Medicine, University of Colorado Anschutz Medical Campus
Jeffrey L. Neul, MD, PhD
Professor of Pediatrics, Division of Neurology, Vanderbilt University Medical Center
Roxana O Carare, PhD
Professor of Neuroanatomy, University of Southampton
Mimoun Azzouz, PhD
Chair of Translational Neuroscience, Director of Gene Therapy Innovation & Manufacturing Centre, IMI ARDAT Coordinator, ERC Advanced Investigator, and Director of MSc Course in Cell & Gene Therapies
University of Sheffield
University of Sheffield